Shares in Mustang Bio soared by as much as 200% Thursday after an experimental gene therapy it holds an exclusive license to proved successful in treating children...

Treatment with Novartis' experimental gene therapy Zolgensma helped to keep alive nearly all infants with a severe form of spinal muscular atrophy who enrolled in ...

A gene therapy developed by St. Jude Children's Research Hospital has shown tremendous promise to change the outlook for children with a debilitating disease that mak...

The SGLT2 inhibitor Jardiance is known to reduce the risk of cardiac death in patients with diabetes, and scientists a...

Cannabidiol (CBD), a non-psychoactive compound in cannabis, is being touted as beneficial for many health conditions, ranging from anxiety to epilepsy. Although much ...

Alnylam Pharmaceuticals on Monday announced a major drug development collaboration with Regeneron, taking its expertise in RNA interference to a new partner as it ...

Audentes Therapeutics has licensed an experimental project from Nationwide Children's Hospital that the company says will stimulate production of a near-complete ...

Since its founding in 2001, the company has spun out and sold two companies: hemophilia-focused Chatham Therapeutics and...

Two separate Nature studies have pinpointed WRN as a promising drug target for MSI tumors. (kirstypargeter/iStock/Gett...

French scientists characterized T cells against Ebola virus among survivors in a finding they believe could guide the ...